So that's a simple genetic disease. If the disease results from the lack
of a gene, then one way to treat the disease would be to give the patient
BACK the gene they're missing. Why would we do this violent step? Gene
therapy may offer cures to incurable diseases. It may also improve
quality of life - diabetics have to sample their blood sugar and take
shots multiple times a day - what if we could fix it in one treatment?
But there are definite risks. The biggest headlines you've seen probably
all say the same thing - trials fail, and patients die. What's going on
here? Tonight, we're going to go behind the hype.
Slide 6