So, gene therapy faces a lot of problems. But what are our current alternatives? While there's a lot of study going into finding safer viruses for gene therapy, for the moment a direct gene therapy approach wouldn't work. We could try to treat them with stem cells, but if the stem cells came from another person, our patient's immune system would reject them. And we could treat them with their OWN stem cells, but their stem cells have the same problem they do, so we would have to fix their cells first. Thus, we have a combination approach - what if we get a person's stem cells and fixed those cells with gene therapy?

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